gene therapy

Partha Nandi, MD
Gene Therapy Helped Adult Retinas Repair Damaged Wiring in New Study
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Gene Therapy Helped Adult Retinas Repair Damaged Wiring in New Study

ByPartha Nandi, MD

For a long time, the accepted view was that the retina’s nerve wiring is set in childhood and that adult nerve cells can be protected but not rebuilt. A new study from Michigan State University challenges that view. With a single dose of gene therapy, researchers restored vision in adult dogs born with an inherited…

What is tRNA? Understanding the New Therapy for Rare Diseases

What is tRNA? Understanding the New Therapy for Rare Diseases

ByPartha Nandi, MD

As a doctor, one of the hardest conversations I have is telling a patient that their genetic condition has no cure. We often spend years just managing symptoms, but recent medical research is shifting focus directly to the root cause. You likely know about mRNA from recent vaccines, but scientists are now looking closely at…

Can One Gene Hold the Key to Stopping Autoimmune Disease?
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Can One Gene Hold the Key to Stopping Autoimmune Disease?

ByPartha Nandi, MD

Imagine if the body’s immune system could be retrained to stop attacking itself. Scientists have identified a gene called Egr1 that may make this possible. This discovery could change how we understand and treat autoimmune diseases such as multiple sclerosis, lupus, and rheumatoid arthritis. Autoimmune diseases occur when the immune system loses its ability to…

First-Ever Successful Huntington’s Disease Treatment Slows Progression by 75 Percent
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First-Ever Successful Huntington’s Disease Treatment Slows Progression by 75 Percent

ByPartha Nandi, MD

For decades, Huntington’s disease has stood as one of medicine’s most heartbreaking diagnoses, a slow and unstoppable decline that robs individuals of movement, memory, and personality. Now, for the first time, scientists have achieved something once thought impossible: slowing the disease’s progression by 75 percent. In early clinical trials, an experimental gene therapy called AMT-130…